Agios Pharmaceuticals is seeking accelerated approval from the U.S. FDA for its oral medication mitapivat for treating sickle ...

Newer oral blood thinners were linked to lower nonmajor bleeding risk than warfarin in adults with sickle cell disease, a ...

Following a reimbursement deal with Vertex, people with SCD in Germany will now have greater access to the gene-editing ...

SCD hospital care varied across New York State, with regional differences in admissions, charges, stays, and severity, a ...

Clinician bias toward people with sickle cell disease (SCD) may be tied to stigma around opioid use, rather than race or chronic pain alone, a new study suggests. “Although patients with sickle cell ...

Having a remote job has been a game-changer for me as someone with sickle cell disease. I’m better able to manage my health — no rushed mornings, cold commutes, or physical strain. I can plan my day ...

The Japan Agency for Medical Research and Development (AMED) — a national funding agency created to support medical R&D in the Asian nation — has awarded up to $32 million to Epifrontier Therapeutics ...

In the U.S., having sickle cell disease (SCD) continues to place a heavy clinical burden on patients, who often require multiple medications, frequent blood transfusions, and the use of opioids to ...

A blood test measuring levels of the protein cystatin C may provide a more reliable way to monitor for kidney problems in children and young adults with sickle cell disease (SCD), a small study ...

The European Medicines Agency (EMA) has confirmed the continuing suspension of marketing authorization for Pfizer’s sickle cell disease (SCD) treatment Oxbryta (voxelotor) — withdrawn from the market ...

An intervention designed to improve adherence to hydroxyurea — by providing extra support from community health workers (CHWs) and daily text reminders — may enhance quality of life for adolescents ...

The investigational gene-editing therapy OTQ923 resulted in normalization of the speed of blood flow in the brain of three adults with sickle cell disease (SCD), according to data from a Phase 1 ...