MedPage Today on MSN
Gene Therapy Restores Hearing for Rare Cause of Congenital Deafness
In a small pivotal trial of an investigational gene therapy, most cases of congenital profound deafness from genetic variants ...
A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...
On her mother’s instruction, a toddler gives her pink stuffed horse, Snap Snap, a big cuddle. Then, as told, she plants a kiss on his soft fur and, because he’s hungry, feeds him a pretend bowl of ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...
Despite announcing a broad pivot to siRNA earlier this year, Sarepta is following through with an investigational gene ...
News-Medical.Net on MSN
Experimental gene therapy restores immune system function in children with genetic immune disorder
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of ...
Zacks Investment Research on MSN
REGN Reports Encouraging Data on Gene Therapy for Genetic Hearing Loss (Revised)
Regeneron Pharmaceuticals, Inc. REGN announced updated data on its investigational gene therapy DB-OTO from the CHORD study.
Huntington’s disease has been successfully treated for the first time using a gene therapy, which may be available in the US ...
Smarter design through targeted delivery and human-relevant testing can save the industry from costly safety failures.
A local gene therapy pioneer is taking on some of the rarest diseases known to medicine with a new venture spun out from his ...
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