In a small pivotal trial of an investigational gene therapy, most cases of congenital profound deafness from genetic variants ...
On her mother’s instruction, a toddler gives her pink stuffed horse, Snap Snap, a big cuddle. Then, as told, she plants a kiss on his soft fur and, because he’s hungry, feeds him a pretend bowl of ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...
Despite announcing a broad pivot to siRNA earlier this year, Sarepta is following through with an investigational gene ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Regeneron Pharmaceuticals, Inc. REGN announced updated data on its investigational gene therapy DB-OTO from the CHORD study.
Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the long-term safety and efficacy of the curative treatment, in a study led by ...
From the 2010s to the present, the existing technologies in the clinic and operating room have been improved with the goals ...
Medication has long been the cornerstone of treatment for people with epilepsy, but it doesn't stop seizures for everyone and ...
When Brianna gave birth to her son Domenic, she never expected to hear the words “hemophilia B.” With no family history of ...
The Xevo CDMS enhances analysis of large biomolecules, crucial for next-gen therapeutics, using individual-particle mass measurement for molecules up to 150+ MDa. Electrostatic Linear Ion Trap (ELIT) ...