The FDA has granted orphan drug designation to the investigational therapy BA-101 for the treatment of patients with ...

The One Big Beautiful Bill Act ("OBBB") expands exemptions for orphan drugs from mandatory Medicare price negotiations and modifies their eligibility timeline. On July 4, 2025, President Trump signed ...

DUBLIN--(BUSINESS WIRE)--The "Orphan Drugs - Global Strategic Business Report" report has been added to ResearchAndMarkets.com's offering. The global market for Orphan Drugs was estimated at US$179.5 ...

Cellectis said a drug it developed is used as part of a treatment regimen for certain leukemia patients received orphan drug designation from the Food and Drug Administration. CLLS52, or alemtuzumab, ...

This month marks the 40th anniversary of the Orphan Drug Act. Since it was signed into law in 1983, the FDA has approved more than 1,100 treatments for rare diseases. The act also created an industry ...

Premiering in 2013, the series starred the then-unknown Tatiana Maslany in a mystery that quickly spun out into a gripping ...

First responders look over the site of an explosion Monday at an orphan well in Independence Township within the Wayne National Forest. The Ohio Department of Natural Resources said Tuesday that ...

Orphan is coming back. According to Variety, a third installment in the horror movie series has been announced by Lionsgate. Isabelle Fuhrman, who played the role of Esther (aka Leena Klammer) in the ...

A new initiative aimed at repairing orphan roads in Onslow County was introduced to the community during a meeting in ...